Puas yog Gene Therapy kis mus rau cov xeeb ntxwv?
Puas yog Gene Therapy kis mus rau cov xeeb ntxwv?

Video: Puas yog Gene Therapy kis mus rau cov xeeb ntxwv?

Video: Puas yog Gene Therapy kis mus rau cov xeeb ntxwv?
Video: Txhob Nco Kuv Lawm Nkauj Hmoob🌹Puas Coos Khem🌹Xis Thoj🌹official MV 2023 2024, Tej zaum
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Kev kho noob caj noob ces tuaj yeem ua tau ncaj qha rau hauv lub cev hlwb (somatic) lossis hauv cov qe lossis cov phev hlwb (germline) kom qhov kev hloov pauv. dhau rau cov tiam tom ntej. Los ntawm kev tsom mus rau cov hlwb somatic, cov genome hloov tab sis qhov kev hloov yuav tsis yog kis mus rau cov xeeb ntxwv.

Hauv qhov no, kev kho noob tau ua tiav?

Cov possibilities ntawm kev kho noob caj noob ces tuav ntau cov lus cog tseg. Clinical trials ntawm kev kho noob caj noob ces nyob rau hauv cov neeg tau qhia ib co kev vam meej hauv kev kho tej yam kab mob, xws li: mob hnyav ua ke tiv thaiv kab mob. Hemophilia.

Ib yam li ntawd, kev kho noob caj noob ces pib li cas? Thawj pom zoo kev kho noob caj noob ces Kev tshawb fawb soj ntsuam hauv Teb Chaws Asmeskas tau tshwm sim rau 14 Cuaj hlis 1990, ntawm National Institutes of Health (NIH), raws li kev coj ntawm William French Anderson. Plaub-xyoo-laus Ashanti DeSilva tau txais kev kho mob rau ib tug caj ces qhov tsis xws luag uas ua rau nws nrog ADA-SCID, lub cev tsis muaj zog tiv thaiv kab mob hnyav.

Tsis tas li ntawd, hom kev kho gene feem ntau yog dab tsi?

Ob Hom Kev Kho Mob Gene Qhov no yog qhov ntau hom kev kho gene ua ua. Kab mob kev kho noob caj noob ces , uas yuav hloov kho cov noob nyob rau hauv qe los yog phev hlwb, uas yuav kis tau ib yam caj ces hloov mus rau tiam tom ntej.

Puas yog Gene Therapy yav tom ntej?

Lub peev xwm lub zog ntawm kev kho noob caj noob ces Feem ntau kev kho noob caj noob ces rau cov kab mob xws li cystic fibrosis thiab hemophilia tau tsim tsuas yog kom yooj yim, tsis kho, tus kab mob. Txawm li cas los xij, kev xa khoom ntawm cov ntawv luam ntawm noob muab ib txoj hauv kev los kho tus kab mob ntawm nws cov theem pib.

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